Adrenoleukodystrophy is a rare condition associated with abnormalities in myelin, the white matter that protects nerve fibers in the spinal cord and brain. It occurs due to a mutation on the X ...

Please provide your email address to receive an email when new articles are posted on . Treatment with leriglitazone showed disease arrest in seven of 20 patients. The treatment was generally ...

Cerebral ALD can occur at any age and is most likely defined by the interplay between the primary ABCD1 mutation, a multitude of genetic variants and environmental ...

Neonatal adrenoleukodystrophy (NALD) is the former name of a rare genetic disorder known as Zellweger spectrum disorder (ZSD). Doctors usually diagnose it shortly after birth, and treatment includes ...

X-linked adrenoleukodystrophy is a rare genetic condition that causes problems with the white matter in your nervous system and adrenal glands. X-linked adrenoleukodystrophy (X-ALD) is a genetic ...

X-linked adrenoleukodystrophy (X-ALD) is a debilitating disease caused by mutations in the ABCD1 gene. Approximately 30% of affected boys develop the progressive ...

Adrenoleukodystrophy (ALD) is rare X-linked genetic disease that affects the adrenal glands (found on top of the kidneys) as well as the myelin in the brain and spinal cord. The incidence of ALD is ...

Cerebral adrenoleukodystrophy (CALD) is a rare progressive, genetic brain disease that primarily presents in young boys, causing loss of neurological function and ultimately leading to early death.

Please provide your email address to receive an email when new articles are posted on . The FDA granted accelerated approval to bluebird bio Inc for elivaldogene autotemcel, its gene therapy that aims ...

(MENAFN- GlobeNewsWire - Nasdaq) The global adrenoleukodystrophy market is in a growth stage, driven by advancements in gene and drug therapies, improved diagnostic capabilities like newborn screening ...

X-linked adrenoleukodystrophy (X-ALD) is caused by a defect in the gene ABCD1, which maps to Xq28 and codes for a peroxisomal membrane protein that is a member of the ...

We conducted a randomized, double-blind, placebo-controlled, crossover trial comparing lovastatin at a dose of 40 mg once daily with placebo (Current Controlled Trials number, ISRCTN31565393). Outcome ...